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STAT+: BridgeBio drug for genetic cause of dwarfism succeeds in key study
Stat News|2/12/2026
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rare diseases
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2026-01-262026-02-12
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Opinion: My granddaughter has a rare disease. But clinical trials often exclude patients like her
Stat News|2/11/2026
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STAT+: FDA’s new ‘plausible mechanism pathway’ for personalized gene editing raises concerns
Stat News|1/26/2026