UNVERIFIEDSingle Source
STAT+: FDA approves Rocket gene therapy for rare immune disorder
Stat News|3/27/2026
GT
Gene therapy
16 stories tracked
Executive summary being generated...
Lindy
0
Breaking
0
Unverified
8
Activity (Last 30 Days)
1
2026-03-272026-03-27
Top Publishers
Stat News8 stories
Stories (Latest First)
UNVERIFIEDSingle Source
STAT+: FDA is ‘not convinced’ UniQure’s Huntington’s therapy has benefit, senior official says
Stat News|3/3/2026
UNVERIFIEDSingle Source
Opinion: I’m a rare disease mom, and I finally have new hope for my son’s future
Stat News|2/27/2026
UNVERIFIEDSingle Source
STAT+: FDA Commissioner Marty Makary defends rare disease drug rejections, Vinay Prasad
Stat News|2/26/2026
UNVERIFIEDSingle Source
STAT+: FDA unveils rules for bespoke gene therapies, predicting flood of rare disease applications
Stat News|2/23/2026
UNVERIFIEDSingle Source
STAT+: Vertex’s CRISPR treatment for sickle cell disease hits unexpected roadblock
Stat News|2/5/2026
UNVERIFIEDSingle Source
STAT+: FDA’s new ‘plausible mechanism pathway’ for personalized gene editing raises concerns
Stat News|1/26/2026